Real-world outcomes of Voretigene Neparvovec: a single-centre consecutive case series

Jalil, Assad; Ferrara, Mariantonia; Lippera, Myrta; Parry, Neil; C Black, Graeme; Banderas, Sandra; Ashworth, Jane; Biswas, Sus; Hall, Georgina; Gray, Jane; Newman, William; Ivanova, Tsveta